Gene Therapy Mind Map

On Rare Disease Day, we at P4A are exploring the most innovative ways to treat and cure rare diseases. This has led  to the creation of a Gene Therapy Mind Map, a learning resource to understand the different types and benefits of gene therapy. What is a Gene Therapy mind map? The Gene Therapy Mind…

Dear orphan drug industry, are you prepared?

Rare Disease Day infographic – US & EU February 28 is rare disease day. To be rare is to be unique. And a rare disease area requires an innovative solution to access. To commemorate this day, Partners4Access are publishing two infographics focusing on key aspects that impact commercialization of orphan drugs. The infographics capture three…

P4A attends the Festival of Genomics in Boston

Partners4Access will attend the Festival of Genomics in Boston on October 3rd, 2017. Sophie Schmitz, Managing Partner at P4A will be there meeting representatives of the research and patient community as well as the pharmaceutical industry. The Festival celebrates the achievements made within genomics and human health. The 1200 attendees aim to “shape ideas, challenge…

P4A participated at the Vecht voor Kinderen Rally

At the weekend (17/06), Sophie participated in the Dutch Vecht voor Kinderen Rally (fight for children rally), supporting a number of children charities including a children’s hospice, child cancer organisation that provides children with wigs and various development programmes in Africa. Those sponsoring and charity activities have a long tradition  at Partners4Access, in particular supporting…

Sophie Schmitz attended world orphan drug congress

Many rare disease patients lay their hope in gene-therapy development. However, recent experience with Glybera (uniQure) has shown difficulties faced in the launch and access. During the World Orphan Drug Congress in Washington this month, Partners4Access had the opportunity to get latest insights from a German sickness fund that reimbursed Glybera and the CEO of…