Leading industry conversations through
world-class knowledge on orphan drugs,
cell and gene therapies

We apply enlightened thinking to the issues facing the rare disease
community. Through our insights, opinions, views and predictions, P4A
produce industry influencing thought leadership in the following areas



In hour-long, quarterly broadcasted industry stakeholder discussions, P4A experts tackle complex subjects such as gene therapy and emerging technologies that influence and shape industry-wide conversations

Podcast - Let’s Talk Rare

Monthly podcasts highlighting the most important news developments and impacts on the orphan drug, cell and gene therapy world including research advancements, corporate events and regulatory changes


P4A experts regularly share their unique perspectives that inform and challenge the norm through articles and whitepapers. Read insights ranging from Hospital Exemptions to Innovative Access Agreements


P4A’s contributors share their expert views on individual subjects that are having an effect in the orphan drugs space. Blogs cover a huge range of topics that address news and challenge current Pharma thinking