Analyzing unmet need ahead of trial design and launch

Price Optimisation, Value Communication

The combination of medical and access professionals within P4A helped us to better communicate the unmet need and burden of disease ahead of launch.

Global Access Lead

Client Challenge

Assessing whether value perception differed across patient population segments.

A rare disease biotech company approached us to support understanding of the price potential of their asset

They were keen to understand if the value perception differed across patient population segments: highly vs moderately vs not transfusion dependent.

P4A Solution

P4A analyzed the Anaemia landscape and perceptions of payers. We noticed fatigue, a key symptom of anaemia was:

extremely heterogenous
misunderstood

We recommended to develop a test battery with questions to assess the patients’ perceived need which can be validated in clinical trials moving forward

The Successful Outcome

The client was able to communicate the value of its asset and drive access for a broader group of patients, all in dire need of a new treatment option.

Once payers understood the burden of extreme fatigue, they were less likely to consider restricting to a transfusion dependent patient population.

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Analyzing unmet need ahead of trial design and launch

Client Challenge

Assessing whether value perception differed across patient population segments.

P4A Solution

P4A analyzed the Anaemia landscape and perceptions of payers. We noticed fatigue, a key symptom of anaemia was:

The Successful Outcome

The client was able to communicate the value of its asset and drive access for a broader group of patients, all in dire need of a new treatment option.

Need more details?

Explore other case studies

Understand evidence requirements beyond clinical trial data for launching an orphan drug in Türkiye & the GCC

Optimising the PRMA potential of an orphan oncology asset in EU4 + UK and Japan

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Analyzing unmet need ahead of trial design and launch

Client Challenge

Assessing whether value perception differed across patient population segments.

P4A Solution

P4A analyzed the Anaemia landscape and perceptions of payers. We noticed fatigue, a key symptom of anaemia was:

The Successful Outcome​

The client was able to communicate the value of its asset and drive access for a broader group of patients, all in dire need of a new treatment option.

Need more details?

Explore other case studies

Understand evidence requirements beyond clinical trial data for launching an orphan drug in Türkiye & the GCC

Optimising the PRMA potential of an orphan oncology asset in EU4 + UK and Japan

About

Services

Insights

Case Studies

Contact

P4A Services

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The Successful Outcome